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Tag: Rare Diseases

Clinical Development

Patient-Focused Clinical Trial Design for Rare Diseases – Part 1

  • June 13, 2018

A few months ago, Medpace and the Cincinnati Children’s Hospital Medical Center presented a webinar on the importance of patient-centric clinical research. Over the next…

Clinical Development

Q&A with Dr. Richard Scheyer: Novel Approaches to Confirming CNS Penetration and Target Engagement

  • May 29, 2018

Richard Scheyer, MD, Vice President, Medical Affairs at Medpace answers some questions about his upcoming presentation about CNS-targeted therapies at DIA 2018.

Clinical Development

How Rare Diseases Are Showing the Way Toward Precision Medicine – Part 3

  • April 18, 2018

In our previous post, we discussed the approaches to help you identify, enroll and retain rare disease populations in clinical trials. Once the right patients…

Clinical Development

How to Identify, Enroll, and Retain Rare Disease Populations in Clinical Trials

  • February 20, 2018

Enrolling enough subjects into a rare disease study can seem like an insurmountable challenge, especially when you're looking at a subset of a rare disease,…

Clinical Development

How Rare Diseases Are Showing the Way Toward Precision Medicine – Part 1

  • December 19, 2017

In Part 1 of a 3 part blog series, we will explore how the heritability of neurological diseases and psychiatric diseases is changing the clinical…

Clinical Development

Duchenne Muscular Dystrophy: Challenges in Clinical Research

  • October 30, 2017

Duchenne Muscular Dystrophy (DMD) is a specific type of muscular dystrophy characterized by muscle weakness and deterioration. DMD research comes with its fair share of…

Central Laboratories

Biomarkers for Celiac Disease Clinical Trials

  • October 2, 2017

As a full service, global CRO with an integrated central lab, Medpace has the scientific, operational and regulatory expertise to manage your celiac disease clinical…

Clinical Development

How important is patient-centricity in rare disease studies?

  • September 6, 2017

Patient-centricity is becoming increasingly important in all areas, but particularly in rare diseases. In this post, Dr. Richard Scheyer discusses the importance of patient-centricity in…

Clinical Development

How to Leverage Research Networks to Accelerate Orphan Drug Development

  • August 7, 2017

In this post, Dr. Terence Eagleton highlights the growing interest in the development of products in the rare disease space, the unique challenges involved, and…