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Strategies for driving success in NPC clinical trials
Strategies for driving success in NPC clinical trials
Successful Approaches in Global Phase III Ultra-Rare Disease Trial for the Treatment of NPC
In a newly released case study, Medpace rare disease experts explore the challenges of clinical trials for the treatment of Niemann–Pick disease type C.
Download the case study to discover strategic approaches to NPC trials, including strategies for recruitment, endpoint protection, maintaining timelines for database lock, and IP management.

Rare Disease CRO
Innovative Patient Enrollment & Retention Approaches
Rare disease clinical trials present a unique set of challenges in terms of clinical trial design, regulatory strategy, site selection, patient enrollment, and project management. These trials demand a highly experienced, full-service CRO with innovative strategies to identify and engage sites and scarce patient populations, and with expertise in site and project management to achieve study aims.
Accelerate your rare disease trial by partnering with our experienced team of cross-functional experts with innovative study approaches and strong site relationships.